X
Search Filters
Format Format
Subjects Subjects
Subjects Subjects
X
Sort by Item Count (A-Z)
Filter by Count
index medicus (18) 18
animals (13) 13
dystrophin (13) 13
duchenne muscular dystrophy (12) 12
exon skipping (11) 11
muscular dystrophy, duchenne - genetics (11) 11
dystrophin - genetics (9) 9
muscular dystrophy (9) 9
exons (8) 8
humans (8) 8
male (8) 8
muscular dystrophy, duchenne - therapy (8) 8
mutation (8) 8
proteins (8) 8
duchenne muscular-dystrophy (7) 7
duchenne's muscular dystrophy (7) 7
dystrophy (7) 7
medicine, research & experimental (7) 7
congenital, hereditary, and neonatal diseases and abnormalities (6) 6
expression (6) 6
female (6) 6
gene expression (6) 6
mice (6) 6
multidisciplinary sciences (6) 6
musculoskeletal diseases (6) 6
rescue (6) 6
antisense oligonucleotides (5) 5
disease models, animal (5) 5
dmd gene (5) 5
dogs (5) 5
exons - genetics (5) 5
genetics & heredity (5) 5
muscle, skeletal - pathology (5) 5
oligonucleotides, antisense - genetics (5) 5
skeletal muscle (5) 5
skeletal-muscle (5) 5
alternative splicing (4) 4
becker muscular dystrophy (4) 4
biochemistry & molecular biology (4) 4
cells (4) 4
medicine (4) 4
morpholinos - genetics (4) 4
muscle pathology (4) 4
muscle, skeletal - metabolism (4) 4
muscular dystrophy, duchenne - metabolism (4) 4
musculoskeletal system (4) 4
oligomers (4) 4
oligonucleotides (4) 4
phenotype (4) 4
restoration (4) 4
rna, messenger - metabolism (4) 4
rodents (4) 4
systemic delivery (4) 4
toxicity (4) 4
amino acid sequence (3) 3
analysis (3) 3
antisense oligonucleotide (3) 3
biochemistry (3) 3
biotechnology & applied microbiology (3) 3
cardiomyopathy (3) 3
degeneration (3) 3
dentistry (3) 3
dystrophin - metabolism (3) 3
eteplirsen (3) 3
gene (3) 3
gene expression regulation (3) 3
genetic research (3) 3
genetic therapy (3) 3
horse (3) 3
horses - genetics (3) 3
human necessities (3) 3
hygiene (3) 3
isoenzymes (3) 3
mdx52 mice (3) 3
medical or veterinary science (3) 3
medical research (3) 3
messenger-rna (3) 3
mice, inbred mdx (3) 3
molecular sequence data (3) 3
morpholinos (3) 3
mrna expression (3) 3
muscles (3) 3
muscular dystrophy, duchenne - pathology (3) 3
original (3) 3
physiological aspects (3) 3
preparations for medical, dental, or toilet purposes (3) 3
protein (3) 3
research article (3) 3
review (3) 3
rna (3) 3
science (3) 3
skeletal (3) 3
skeletal-muscles (3) 3
adult (2) 2
aging (2) 2
aging - genetics (2) 2
amino acids (2) 2
animal models (2) 2
article (2) 2
base sequence (2) 2
more...
Language Language
Publication Date Publication Date
Click on a bar to filter by decade
Slide to change publication date range


PLoS ONE, ISSN 1932-6203, 03/2015, Volume 10, Issue 3, pp. e0120058 - e0120058
Journal Article
Proceedings of the National Academy of Sciences of the United States of America, ISSN 0027-8424, 04/2017, Volume 114, Issue 16, pp. 4213 - 4218
Duchenne muscular dystrophy (DMD) is a lethal genetic disorder caused by an absence of the dystrophin protein in bodywide muscles, including the heart.... 
Cardiac Purkinje fibers | Dystrophic dog model | Peptide-conjugated morpholinos | Duchenne muscular dystrophy | Exon skipping | MUSCLE PATHOLOGY | MULTIDISCIPLINARY SCIENCES | DMD GENE | CARDIOMYOPATHY | BODYWIDE | dystrophic dog model | peptide-conjugated morpholinos | MDX52 MICE | OLIGONUCLEOTIDES | RESCUE | exon skipping | LABORATORY-ANIMALS | cardiac Purkinje fibers | EXPRESSION | EXONS 45-55 | Genetic Therapy | Muscular Dystrophy, Animal - genetics | Exons | Male | Muscle, Skeletal - metabolism | Muscular Dystrophy, Animal - complications | Muscular Dystrophy, Duchenne - complications | Cardiomyopathies - etiology | Cardiomyopathies - therapy | Cell-Penetrating Peptides - pharmacology | Animals | Dogs | Morpholinos - pharmacology | Female | Muscular Dystrophy, Animal - therapy | Muscle, Skeletal - pathology | Muscular Dystrophy, Duchenne - genetics | Muscular Dystrophy, Duchenne - therapy | Dystrophin - metabolism | Disease Models, Animal | Heart | Physiological aspects | Health aspects | Conduction | Intravenous administration | Peptides | Toxicity | Cardiomyopathy | Effects | Muscular dystrophy | Fibers | Oligomers | Nerve conduction | Arginine | Duchenne's muscular dystrophy | Degeneration | Polymers | Heart diseases | Dystrophin | EKG | Cardiac muscle | Abnormalities | Muscles | Skeletal muscle | Purkinje fibers | Myocardium | Dystrophy | Index Medicus | Biological Sciences
Journal Article
Journal Article
Molecular Therapy, ISSN 1525-0016, 11/2017, Volume 25, Issue 11, pp. 2561 - 2572
Duchenne muscular dystrophy (DMD), the most common lethal genetic disorder, is caused by mutations in the ( ) gene. Exon skipping is a therapeutic approach... 
mdx52 mice | Becker muscular dystrophy | Exondys 51 | eteplirsen | exon skipping | Duchenne muscular dystrophy | clinical trial candidate screening | BMD | antisense morpholino | drisapersen | machine learning | hDMD/Dmd-null mice | MEDICINE, RESEARCH & EXPERIMENTAL | DIAGNOSIS | DESIGN | EFFICACY | DMD GENE | RESTORATION | PHASE-2 | OLIGONUCLEOTIDES | THERAPY | BIOTECHNOLOGY & APPLIED MICROBIOLOGY | GENETICS & HEREDITY | MICE | ETEPLIRSEN | Exons | Humans | Oligonucleotides, Antisense - metabolism | Male | Muscle, Skeletal - metabolism | Reading Frames | Recovery of Function | RNA Splicing | Female | Muscular Dystrophy, Duchenne - therapy | Dystrophin - metabolism | Disease Models, Animal | Gene Expression | Morpholinos - genetics | Mice, Transgenic | Muscular Dystrophy, Duchenne - pathology | Morpholinos - metabolism | Animals | Oligonucleotides, Antisense - genetics | Dystrophin - genetics | Mice | Muscular Dystrophy, Duchenne - metabolism | Muscle, Skeletal - pathology | Muscular Dystrophy, Duchenne - genetics | Mutation | Genetic Therapy - methods | Performance evaluation | Medical research | Statistical analysis | Splicing | Antisense oligonucleotides | Muscular dystrophy | Proteins | Musculoskeletal system | Protein folding | Efficiency | Exon skipping | Duchenne's muscular dystrophy | Protein expression | Muscle function | Dystrophy | Dystrophin | Evacuations & rescues | Index Medicus | hDMD | Dmd-null mice | Original
Journal Article
Journal Article
Molecular Therapy - Nucleic Acids, ISSN 2162-2531, 2015, Volume 4, Issue 2, pp. e225 - e225
Antisense-mediated exon skipping, which can restore the reading frame, is a most promising therapeutic approach for Duchenne muscular dystrophy. Remaining... 
multiexon skipping | antisense therapeutics | mdx52 mouse | dystrophin | Vivo-Morpholinos | Duchenne muscular dystrophy | Antisense therapeutics | Dystrophin | Multiexon skipping | Mmdx52 mouse | MUSCLE PATHOLOGY | MEDICINE, RESEARCH & EXPERIMENTAL | CARDIAC-MUSCLE | RESTORATION | DETERMINES | THERAPY | RESCUE | IMPROVEMENT | DUCHENNE MUSCULAR-DYSTROPHY | SKELETAL | EXPRESSION | Original
Journal Article
PLoS ONE, ISSN 1932-6203, 07/2013, Volume 8, Issue 7, pp. e69194 - e69194
Journal Article