X
Search Filters
Format Format
Subjects Subjects
Subjects Subjects
X
Sort by Item Count (A-Z)
Filter by Count
index medicus (13) 13
humans (11) 11
male (10) 10
child (7) 7
child, preschool (6) 6
clinical trials (6) 6
disease progression (6) 6
duchenne muscular dystrophy (6) 6
female (6) 6
muscles (6) 6
6-minute walk test (5) 5
age (5) 5
biomarkers (5) 5
duchenne's muscular dystrophy (5) 5
dystrophy (5) 5
mri (5) 5
muscle, skeletal - pathology (5) 5
muscular dystrophy (5) 5
mutation (5) 5
pediatrics (5) 5
proteins (5) 5
abridged index medicus (4) 4
article (4) 4
children & youth (4) 4
clinical neurology (4) 4
infant (4) 4
magnetic resonance imaging (4) 4
magnetic resonance spectroscopy (4) 4
muscular dystrophy, duchenne - pathology (4) 4
muscular dystrophy, duchenne - physiopathology (4) 4
natural history (4) 4
neurology (4) 4
skeletal muscle (4) 4
adolescent (3) 3
babies (3) 3
boys (3) 3
children (3) 3
cohort studies (3) 3
double-blind method (3) 3
drug dosages (3) 3
end-points (3) 3
longitudinal studies (3) 3
medical research (3) 3
medicine (3) 3
medicine and health sciences (3) 3
medicine, general & internal (3) 3
medicine, research & experimental (3) 3
muscle, skeletal - physiopathology (3) 3
neurosciences (3) 3
patients (3) 3
physiology (3) 3
quantification (3) 3
research article (3) 3
smn protein (3) 3
spinal muscular atrophy (3) 3
tissue (3) 3
trial (3) 3
age of onset (2) 2
analysis (2) 2
antisense oligonucleotides (2) 2
bioindicators (2) 2
care and treatment (2) 2
cell survival (2) 2
correlation analysis (2) 2
cross-sectional studies (2) 2
death (2) 2
development and progression (2) 2
diagnostic medicine (2) 2
diagnostic radiology (2) 2
drug therapy (2) 2
general & internal medicine (2) 2
genetics (2) 2
genetics & heredity (2) 2
hereditary diseases (2) 2
image processing, computer-assisted (2) 2
infants (2) 2
injections, spinal (2) 2
leg (2) 2
leg - pathology (2) 2
lipids (2) 2
magnetic resonance imaging - methods (2) 2
mortality (2) 2
motor skills (2) 2
motor task performance (2) 2
mrna (2) 2
multicenter (2) 2
multidisciplinary sciences (2) 2
muscular dystrophy, duchenne - diagnostic imaging (2) 2
muscular dystrophy, duchenne - drug therapy (2) 2
musculoskeletal system (2) 2
natural-history (2) 2
neuromuscular diseases (2) 2
oligonucleotides - adverse effects (2) 2
oligonucleotides - therapeutic use (2) 2
oligonucleotides, antisense - adverse effects (2) 2
oligonucleotides, antisense - therapeutic use (2) 2
outcome measure (2) 2
pediatrik (2) 2
pharmacokinetics (2) 2
physical therapy (2) 2
more...
Language Language
Publication Date Publication Date
Click on a bar to filter by decade
Slide to change publication date range


PloS one, ISSN 1932-6203, 2014, Volume 9, Issue 9, pp. e106435 - e106435
Journal Article
PLoS ONE, ISSN 1932-6203, 03/2018, Volume 13, Issue 3, pp. e0194283 - e0194283
Journal Article
by McDonald, Craig M and Campbell, Craig and Torricelli, Ricardo Erazo and Finkel, Richard S and Flanigan, Kevin M and Goemans, Nathalie and Heydemann, Peter and Kaminska, Anna and Kirschner, Janbernd and Muntoni, Francesco and Osorio, Andrés Nascimento and Schara, Ulrike and Sejersen, Thomas and Shieh, Perry B and Sweeney, H Lee and Topaloglu, Haluk and Tulinius, Már and Vilchez, Juan J and Voit, Thomas and Wong, Brenda and Elfring, Gary and Kroger, Hans and Luo, Xiaohui and McIntosh, Joseph and Ong, Tuyen and Riebling, Peter and Souza, Marcio and Spiegel, Robert J and Peltz, Stuart W and Mercuri, Eugenio and Alfano, Lindsay N and Eagle, Michelle and James, Meredith K and Lowes, Linda and Mayhew, Anna and Mazzone, Elena S and Nelson, Leslie and Rose, Kristy J and Abdel-Hamid, Hoda Z and Apkon, Susan D and Barohn, Richard J and Bertini, Enrico and Bloetzer, Clemens and de Vaud, Lausanne Canton and Butterfield, Russell J and Chabrol, Brigitte and Chae, Jong-Hee and Jongno-gu, Daehak-ro and Comi, Giacomi Pietro and Darras, Basil T and Dastgir, Jahannaz and Desguerre, Isabelle and Escobar, Raul G and Finanger, Erika and Guglieri, Michela and Hughes, Imelda and Iannaccone, Susan T and Jones, Kristi J and Karachunski, Peter and Kudr, Martin and Lotze, Timothy and Mah, Jean K and Mathews, Katherine and Nevo, Yoram and Parsons, Julie and Péréon, Yann and de Queiroz Campos Araujo, Alexandra Prufer and Renfroe, J Ben and de Resende, Maria Bernadete Dutra and Ryan, Monique and Selby, Kathryn and Tennekoon, Gihan and Vita, Giuseppe and Clinical Evaluator Training Grp and ACT DMD Study Grp and Clinical Evaluator Training Group and ACT DMD Study Group
The Lancet, ISSN 0140-6736, 09/2017, Volume 390, Issue 10101, pp. 1489 - 1498
Journal Article
Annals of Neurology, ISSN 0364-5134, 12/2017, Volume 82, Issue 6, pp. 883 - 891
Journal Article
Journal Article
Neurology, ISSN 0028-3878, 09/2014, Volume 83, Issue 11, pp. 974 - 980
Journal Article
EMBO Molecular Medicine, ISSN 1757-4676, 01/2013, Volume 5, Issue 1, pp. 80 - 91
Journal Article
Pediatrics in Review, ISSN 0191-9601, 05/2016, Volume 37, Issue 5, pp. 218 - 219
Journal Article
Journal of Neuromuscular Diseases, ISSN 2214-3599, 2019, Volume 6, Issue 1, pp. 43 - 54
Edasalonexent is an orally administered small molecule designed to inhibit NF-κB, which is activated from infancy in Duchenne muscular dystrophy and is central... 
NF-κ B | edasalonexent | CAT-1004 | Duchenne muscular dystrophy | NF-κB protein | Pediatrics | Pharmacodynamics | Duchenne's muscular dystrophy | Oral administration | Diarrhea | Dystrophy | Pharmacokinetics | Males | Serum proteins | Patients | Muscular dystrophy
Journal Article