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Journal Article
Molecular Genetics and Metabolism, ISSN 1096-7192, 02/2015, Volume 114, Issue 2, pp. S53 - S53
Journal Article
Molecular Genetics and Metabolism, ISSN 1096-7192, 07/2012, Volume 106, Issue 3, pp. 330 - 344
Journal Article
Journal Article
Molecular Genetics and Metabolism, ISSN 1096-7192, 01/2017, Volume 120, Issue 1-2, pp. S140 - S140
Journal Article
Molecular Genetics and Metabolism, ISSN 1096-7192, 01/2017, Volume 120, Issue 1-2, pp. S127 - S127
Journal Article
Expert Review of Clinical Pharmacology, ISSN 1751-2433, 12/2016, Volume 9, Issue 12, pp. 1521 - 1532
Introduction: Morquio A syndrome is a rare, autosomal recessive, lysosomal storage disorder caused by a deficiency in the enzyme... 
GALNS | MPS IVA | enzyme replacement therapy | Elosulfase alfa | Morquio A | mucopolysaccharidosis | lysosomal storage disorder | SAFETY | DISEASE TYPE-A | SPINAL-CORD | PHASE-III TRIAL | RESPIRATORY-FUNCTION | CORD COMPRESSION | PHARMACOLOGY & PHARMACY | PHYSICAL-ACTIVITY | STEM-CELL TRANSPLANTATION
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Journal Article
Molecular Genetics and Metabolism, ISSN 1096-7192, 02/2019, Volume 126, Issue 2, pp. S111 - S111
Journal Article
Molecular Genetics and Metabolism, ISSN 1096-7192, 02/2019, Volume 126, Issue 2, pp. S138 - S139
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Molecular Genetics and Metabolism, ISSN 1096-7192, 02/2019, Volume 126, Issue 2, pp. S71 - S71
Journal Article
Molecular Genetics and Metabolism, ISSN 1096-7192, 01/2017, Volume 120, Issue 1-2, pp. S115 - S115
Journal Article
Expert review of clinical pharmacology, 12/2016, Volume 9, Issue 12, p. 1521
Morquio A syndrome is a rare, autosomal recessive, lysosomal storage disorder caused by a deficiency in the enzyme N-acetylgalactosamine-6-sulfatase (GALNS).... 
Chondroitinsulfatases - adverse effects | Enzyme Replacement Therapy - methods | Humans | Chondroitinsulfatases - therapeutic use | Mucopolysaccharidosis IV - drug therapy | Chondroitinsulfatases - pharmacokinetics
Journal Article
Molecular Genetics and Metabolism, ISSN 1096-7192, 02/2018, Volume 123, Issue 2, pp. S61 - S61
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