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Cancer Research, ISSN 0008-5472, 07/2016, Volume 76, Issue 14 Supplement, pp. CT020 - CT020
The majority of metastatic cancers remain incurable since the current methods of treatment often fail to target the heterogeneous nature of each individual... 
Journal Article
Blood, ISSN 0006-4971, 11/2013, Volume 122, Issue 21, pp. 165 - 165
Abstract Background Suicide gene therapy applied to allogeneic hematopoietic stem cell transplantation (allo-HSCT) is one of the widest clinical applications... 
Journal Article
Molecular Therapy - Methods & Clinical Development, ISSN 2329-0501, 2015, Volume 2, p. 14061
Gene transfer to hematopoietic stem cells with integrating vectors not only allows sustained correction of monogenic diseases but also tracking of individual... 
MEDICINE, RESEARCH & EXPERIMENTAL
Journal Article
Molecular Therapy, ISSN 1525-0016, 09/2012, Volume 20, Issue 9, pp. 34 - 34
We previously reported high frequency hepatocellular carcinoma (HCC) development in mice treated with EIAV SMART2/3 based non-primate lentivirus vectors... 
Journal Article
Journal Article
Blood, ISSN 0006-4971, 11/2011, Volume 118, Issue 21, pp. 165 - 165
Abstract Abstract 165FN2 CB and KB contributed equally and should be considered aequo loco. Wiskott-Aldrich-Syndrome (WAS) is a rare and life-threatening... 
Journal Article
by Seymour, LW and Antoniou, M and Harbottle, Dr Richard P and Denning, C and Hajjar, R and Ferber, S and Searle, P F and Farzaneh, F and Krishnamurthy, P and Tye, G-J and Amofah, E and Barber, L and Chan, L and Mufti, GJ and Noble, A and Harrison, P and Falahati, Rustom and Zhang, Jianqing and Shi, Yimin and Flebbe-Rehwaldt, Linda and Gerson, Stanton L and Gaensler, Karin M L and Wilson, James M and von Kalle, C and Ivics, Z and Ammar, I and Voigt, K and Gogol-Döring, A and Miskey, C and Chen, W and Izsvák, Z and Cathomen, T and Cathomen, T and Jonuschies, J and Boldrin, L and Thrasher, A and Morgan, JE and Muntoni, F and Thrasher, A and Griesenbach, U and Weiss, D and Frances, K and Vassaux, G and Lombardo, A and Cesana, D and Cesana, D and Cesana, D and Cesana, D and Cesana, D and Genovese, P and Genovese, P and Genovese, P and Provasi, E and Colombo, DF and Neri, M and Magnani, Z and Cantore, C and Riso, P Lo and Damo, M and Holmes, MC and Holmes, MC and Gregory, PD and Gritti, A and Bonini, C and Naldini, L and Yáñez-Muñoz, RJ and Biffi, A and Sessa, M and Montini, E and Montini, E and Montini, E and Montini, E and Naldini, L and Wilson, James M and Baum, C and Modlich, U and Schambach, A and Galla, M and Maetzig, T and Kustikova, O and Brugman, M and Suerth, J and Heckl, D and Schwarzer, A and English, R and Wilson, J and Kernan, F and Meivar-Levy, I and Chernichovsky, E and Litichever, N and Ron, K and Sapir, T and Molakandov, K and Docherty, K and Lima, M João and Muir, K and Rashid, ST and Yusa, K and Strick-Marchand, H and Lomas, DA and ...
Human Gene Therapy, ISSN 1043-0342, 10/2011, Volume 22, Issue 10, pp. A1 - A138
Journal Article
Rare Diseases, ISSN 2167-5511, 01/2014, Volume 2, Issue 1, p. e947749
Wiskott-Aldrich-Syndrome (WAS) is a rare X-linked recessive disease caused by mutations of the WAS gene. It is characterized by immunodeficiency, autoimmunity,... 
insertional mutagenesis | leukemia | Wiskott-Aldrich-Syndrome | gene therapy | immunodeficiency
Journal Article
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