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Acta Neuropathologica, ISSN 0001-6322, 1/2018, Volume 135, Issue 1, pp. 95 - 113
Journal Article
Neural Regeneration Research, ISSN 1673-5374, 6/2019, Volume 14, Issue 6, pp. 931 - 938
Journal Article
Molecular Therapy, ISSN 1525-0016, 03/2013, Volume 21, Issue 3, pp. 505 - 506
...), and extensive vacuolation of the central nervous system (CNS) white matter.5 Currently there is no established therapy that affects progression of the disease, and survival is based primarily on improved general medical care... 
MEDICINE, RESEARCH & EXPERIMENTAL | BIOTECHNOLOGY & APPLIED MICROBIOLOGY | MUTATION | GENETICS & HEREDITY | NEURONS | CENTRAL-NERVOUS-SYSTEM | MODEL | ASTROCYTES | BRAIN | DELIVERY | Amidohydrolases - metabolism | Dependovirus - genetics | Recombination, Genetic | Amidohydrolases - genetics | Canavan Disease - genetics | Humans | Aspartic Acid - metabolism | Aspartic Acid - analogs & derivatives | Canavan Disease - therapy | Genetic Vectors | Genetic Therapy - methods
Journal Article
Methods in Molecular Biology, ISSN 1064-3745, 2016, Volume 1382, pp. 429 - 465
.... Whether either of these diseases is amendable by gene therapy depends to a large degree on the knowledge of their pathomechanism, availability of the therapeutic gene, vector selection... 
Niemann-Pick disease | Retrovirus | Canavan's disease | Phenylketonuria | AAV | CNS | Gene therapy | Metabolic disorders | Genetic Therapy | Metabolic Diseases - therapy | Clinical Trials as Topic | Humans | Nervous System Diseases - therapy | Canavan’s disease
Journal Article
Journal of the Neurological Sciences, ISSN 0022-510X, 2015, Volume 366, pp. 116 - 124
Journal Article