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Journal Article
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Pediatric Anesthesia, ISSN 1155-5645, 08/2012, Volume 22, Issue 8, pp. 737 - 744
Journal Article
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Journal Article
Drug Design, Development and Therapy, ISSN 1177-8881, 04/2015, Volume 9, pp. 1937 - 1953
Patients with mucopolysaccharidosis IVA (MPS IVA) can present with systemic skeletal dysplasia, leading to a need for multiple orthopedic surgical procedures,... 
Mucopolysaccharidosis IVA | Skeletal dysplasia | HSCT | ERT | Keratan sulfate | HURLER-SYNDROME | CHEMISTRY, MEDICINAL | mucopolysaccharidosis IVA | BONE-MARROW-TRANSPLANTATION | DRUG-DELIVERY SYSTEM | MUCOPOLYSACCHARIDOSIS TYPE-IVA | LYSOSOMAL STORAGE DISORDERS | II HUNTER-SYNDROME | skeletal dysplasia | MAROTEAUX-LAMY-SYNDROME | keratan sulfate | RECOMBINANT N-ACETYLGALACTOSAMINE-6-SULFATE SULFATASE | TERM-FOLLOW-UP | PHARMACOLOGY & PHARMACY | Hematopoietic Stem Cell Transplantation | Enzyme Replacement Therapy | Mucopolysaccharidosis IV - therapy | Humans | Enzymes | Care and treatment | Patient outcomes | Mucopolysaccharidosis | Transplantation | Health aspects | Hematopoietic stem cells | Methods | Heart | Therapy | Pediatrics | N-Acetylgalactosamine | Respiratory function | Deformation | Syngeneic grafts | Genotype & phenotype | Microorganisms | Apnea | Wheelchairs | Bone marrow | Bone dysplasia | Biocompatibility | Trochanter | Activities of daily living | Orthoses | Knee (anatomy) | Patients | Heart valves | Quality of life | Radiography | Pathology | Storage | Radiographs | Stem cells | Chondrocytes | Biomarkers | Scientific imaging | Mass spectrometry | Knee | Yeast | Transplants & implants | Medical services | Bone marrow transplantation | Stem cell transplantation | Pichia pastoris | Sulfates | Sleep disorders | Biomedical materials | Reduction | Skeleton | Lesions | Recombinant | Bone lesions | Medical screening | Chromatography | Hip | Hemopoiesis | Ankle | Lungs | Coronary vessels | Climb | Bone mineral density
Journal Article