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Circulation, 01/2019, Volume 139, Issue 4, pp. 431 - 443
Hereditary transthyretin-mediated (hATTR) amyloidosis is a rapidly progressive, multisystem disease that presents with cardiomyopathy or polyneuropathy. The... 
APOLLO | cardiac amyloidosis | RNA interference | patisiran | cardiomyopathy | hATTR amyloidosis
Journal Article
Neurology, ISSN 0028-3878, 11/2018, Volume 91, Issue 21, pp. e1999 - e2009
OBJECTIVETo assess the natural history and treatment effect on survival among patients with transthyretin-associated familial amyloid polyneuropathy (TTR-FAP)... 
LIVER-TRANSPLANTATION | PATISIRAN | THERAPY | EFFICACY | TAFAMIDIS | SAFETY | LONG-TERM SURVIVAL | EPIDEMIOLOGY | CLINICAL NEUROLOGY
Journal Article
Pharmaceuticals (Basel, Switzerland), ISSN 1424-8247, 04/2019, Volume 12, Issue 2, p. 52
In 2018, the United States Food and Drug Administration (FDA) approved a total of 59 new drugs, three of them (5%) are TIDES (or also, -tides), two... 
pharmaceutical market | drugs | inotersen | peptides | oligonucleotides | Onpattro | patisiran | Tegsedi | Lutathera | dotatate
Journal Article
Expert Opinion on Pharmacotherapy, ISSN 1465-6566, 03/2019, Volume 20, Issue 4, pp. 473 - 481
Background: Hereditary transthyretin-mediated amyloidosis (hATTR amyloidosis) is a progressive, life-threatening disease. Until recently, tafamidis was the... 
indirect treatment comparison | Hereditary transthyretin-mediated amyloidosis | RNA interference | patisiran | tafamidis | TTR-FAP | METAANALYSIS | CLINICAL-TRIAL | TASK-FORCE | SAFETY | CARE DECISION-MAKING | PHARMACOLOGY & PHARMACY
Journal Article
Annual Review of Pharmacology and Toxicology, ISSN 0362-1642, 1/2019, Volume 59, Issue 1, pp. 605 - 630
Journal Article
Journal of Cardiac Failure, ISSN 1071-9164, 03/2019, Volume 25, Issue 3, pp. 154 - 155
Journal Article
Orphanet Journal of Rare Diseases, ISSN 1750-1172, 12/2015, Volume 10, Issue 1, p. 109
Journal Article
Expert Review of Clinical Pharmacology, ISSN 1751-2433, 02/2019, Volume 12, Issue 2, pp. 95 - 99
Journal Article
Annual Review of Medicine, ISSN 0066-4219, 1/2019, Volume 70, Issue 1, pp. 307 - 321
Journal Article
Journal Article